Faculty Members
Neuromuscular Diseases Served
Sponsored Clinical Trials
Investigator Initiated Trials


To help families, clinicians, and scientists speak a common language as they strive towards their shared goal of optimizing research, education, and clinical care for muscular dystrophy and other neuromuscular disorders. 


To be a leader in the development of novel molecular diagnostic and therapeutic approaches for muscular dystrophy and other neuromuscular disorders, and to be an internationally renowned educational and training site for a range of scientists and clinicians who wish to study and treat these disorders.

My little friend Jacob told me his only wish in the universe is a cure for his muscular dystrophy. It's not a question of whether, but when it will be conquered. Let it be for this generation.

—Paul Wellstone