Michael Przybilla, PhD

Dr. Przybilla's research has focused on the development of animal models of lysosomal diseases and has progressed into the development and testing of novel therapies for such diseases including enzyme replacement therapy, small molecule chaperones, gene therapy, and gene editing. Currently, his research is focused on developing a gene therapy that can potentially serve as a platform technology to treat multiple lysosomal diseases. Additionally, Dr. Przybilla is collaborating with several research groups to test conduct preclinical studies for potential therapeutics for several lysosomal diseases.Interests include: Therapeutic development for genetic diseases, with a focus on lysosomal diseases.